Upsher-Smith Laboratories launched DMD treatment Kymbee in the U.S., backed by a support program for patients.

Columnist Shalom Lim attended a musical honoring healthcare professionals and, as someone with Duchenne MD, came away feeling ...

A regimen of three immune-suppressing drugs may improve the effectiveness of gene therapy for people with DMD, research in ...

Columnist Robin Stemple struggles to feel grateful on difficult days with FSHD, but still tries to recognize his many ...

New research shows DMD is marked by abnormalities in muscle development in the womb, supporting the potential of a therapy ...

The holiday season is upon us, and I am already exhausted. I’m well aware of everything I need to do in December, so being this tired already isn’t great. It makes me think about the opening lines of ...

Columnist Betty Vertin's track career ended years ago, but she never stopped lifting weights — only now its the emotional weight of Duchenne.

A Phase 1/2 clinical trial testing SRP-1003 for myotonic dystrophy type 1 is progressing with higher doses as planned.

What is Elevidys for Duchenne muscular dystrophy? Elevidys (delandistrogene moxeparvovec-rokl), previously known as SRP-9001, is a one-time gene therapy approved in the U.S. to treat patients with ...

A Phase 1/2 clinical trial testing SRP-1003, a treatment for myotonic dystrophy type 1 (DM1), is progressing as planned and continues to enroll patients at higher doses. The Phase 1/2 study ...